F.D.A. Sharply Limits Use of Drug Linked to Two Teen Deaths
14 November 2025 at 16:03
A gene therapy for Duchenne muscular dystrophy caused complications to the liver, prompting a review of its use for younger patients.
The drug Elevidys has been central to the business model of Sarepta Therapeutics, a publicly traded company that is worth about $2 billion.

ยฉ Brian Snyder/Reuters